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Shwachman-Diamond Syndrome

Showing 1 - 25 of >10,000

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Shwachman-Diamond Syndrome, Shwachman-Diamond Syndrome-Like Trial in Aurora, Boston, Cincinnati

Recruiting
  • Shwachman-Diamond Syndrome
  • Shwachman-Diamond Syndrome-Like
    • Aurora, Colorado
    • +3 more
    Sep 25, 2023

    Cancer in Inherited Bone Marrow Failure Syndromes

    Recruiting
    • Diamond Blackfan Anemia
    • +4 more
      • Bethesda, Maryland
      • +1 more
      Jan 24, 2023

      Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive, Acute Leukemia in Remission, Acute Lymphoblastic Leukemia

      Active, not recruiting
      • Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive
      • +36 more
      • Buffalo, New York
        Roswell Park Cancer Institute
      Jan 23, 2023

      Baby Detect : Genomic Newborn Screening

      Recruiting
      • Congenital Adrenal Hyperplasia
      • +126 more
        • Liege, Wallonia, Belgium
          CRMN, Hôpital La Citadelle
        Jan 24, 2023

        Bone Marrow Failure Syndrome, Congenital Amegakaryocytic Thrombocytopenia, Congenital Pure Red Cell Aplasia Trial in United

        Recruiting
        • Bone Marrow Failure Syndrome
        • +6 more
        • Los Angeles, California
        • +23 more
        Aug 15, 2022

        Bone Marrow Failure Syndrome, Severe Aplastic Anemia, Severe Congenital Neutropenia Trial in New York (CD34 Stem Cell Selection

        Active, not recruiting
        • Bone Marrow Failure Syndrome
        • +15 more
        • CD34 Stem Cell Selection Therapy
        • New York, New York
          Morgan Stanley Children's Hospital, New York-Presbyterian, Colum
        Jun 17, 2020

        Hurler Syndrome, Fanconi Anemia, Glanzmann Thrombasthenia Trial in Atlanta (Abatacept)

        Completed
        • Hurler Syndrome
        • +14 more
        • Atlanta, Georgia
          Children's Healthcare of Atlanta
        Dec 20, 2019

        Familial Investigations of Childhood Cancer Predisposition

        Recruiting
        • Acute Leukemia
        • +45 more
          • Memphis, Tennessee
            St. Jude Children's Research Hospital
          May 11, 2022

          Mucopolysaccharidosis I, Mucopolysaccharidosis VI, Adrenoleukodystrophy Trial in Denver, Valhalla, Salt Lake City (Human

          Completed
          • Mucopolysaccharidosis I
          • +15 more
          • Human Placental Derived Stem Cell
          • Denver, Colorado
          • +2 more
          Oct 24, 2022

          Accelerated Phase Chronic Myelogenous Leukemia, Adult Acute Lymphoblastic Leukemia in Remission, Adult Acute Myeloid Leukemia in

          Completed
          • Accelerated Phase Chronic Myelogenous Leukemia
          • +77 more
          • fludarabine phosphate
          • +8 more
          • Buffalo, New York
            Roswell Park Cancer Institute
          Sep 16, 2019

          Bone Marrow Failure Syndrome, Thalassemia, Sickle Cell Disease Trial in Gainesville (Thiotepa--single daily dose,

          Recruiting
          • Bone Marrow Failure Syndrome
          • +15 more
          • Thiotepa--single daily dose
          • Thiotepa--escalated dose
          • Gainesville, Florida
            UF Health Shands Children's Hospital
          Jul 8, 2021

          Frail Elderly Syndrome, Chronic Disease Trial in Calgary, Langley, Vancouver (Advance care planning tools)

          Completed
          • Frail Elderly Syndrome
          • Chronic Disease
          • Advance care planning tools
          • Calgary, Alberta, Canada
          • +3 more
          Jan 17, 2022

          Hepatorenal Syndrome Trial in Canada, United States (Terlipressin, Placebo)

          Completed
          • Hepatorenal Syndrome
          • Birmingham, Alabama
          • +63 more
          Nov 4, 2022

          Steroid-refractory Diamond-Blackfan Anemia (DBA) Trial run by the National Heart, Lung, and Blood Institute (NHLBI) (Bitopertin)

          Not yet recruiting
          • Steroid-refractory Diamond-Blackfan Anemia (DBA)
          • Bethesda, Maryland
            National Institutes of Health Clinical Center
          Apr 28, 2023

          Metabolic Disorders, Hematologic, Immune, or Bone Marrow Disorders, Hemoglobinopathies Trial in Canada, United States (Treatment

          Recruiting
          • Metabolic Disorders
          • +3 more
          • Treatment Plan 1: Stratum 1
          • +3 more
          • Phoenix, Arizona
          • +19 more
          Oct 12, 2021

          Craniopharyngioma, Hypothalamic Obesity, Metabolic Syndrome Trial in Vancouver (Hypothalamic Deep Brain Stimulation)

          Withdrawn
          • Craniopharyngioma
          • +2 more
          • Hypothalamic Deep Brain Stimulation
          • Vancouver, British Columbia, Canada
            Leslie and Gordon Diamond Health Center
          Oct 29, 2020

          DIAMOND AF Post-Approval Study

          Recruiting
          • Paroxysmal Atrial Fibrillation
          • DiamondTemp™ Ablation System
          • Winter Park, Florida
          • +1 more
          Jan 19, 2023

          Persistent Atrial Fibrillation, Atrial Fibrillation Trial in Worldwide (Radiofrequency Ablation)

          Recruiting
          • Persistent Atrial Fibrillation
          • Atrial Fibrillation
          • Radiofrequency Ablation
          • Birmingham, Alabama
          • +28 more
          Jan 17, 2023

          Non-Neoplastic Hematologic and Lymphocytic Disorder Trial in United States (procedure, biological, drug, other, radiation)

          Completed
          • Non-Neoplastic Hematologic and Lymphocytic Disorder
          • Allogeneic Bone Marrow Transplantation
          • +11 more
          • Aurora, Colorado
          • +5 more
          Jul 21, 2021

          Abrasion, Dental, Class I Dental Caries Trial (Bioactive Glass Air Abrasion Particles., Diamond Stone.)

          Not yet recruiting
          • Abrasion, Dental
          • Class I Dental Caries
          • Bioactive Glass Air Abrasion Particles.
          • Diamond Stone.
          • (no location specified)
          Oct 24, 2023

          Sars-CoV2 Trial in Paris (blood sample)

          Completed
          • Sars-CoV2
          • blood sample
          • Paris, France
            Hopital Pitié Salpetrière
          Jul 5, 2022

          Angina, Stable Trial in Denmark, Sweden (CADScor®System)

          Recruiting
          • Angina, Stable
          • CADScor®System
          • Copenhagen S, Denmark
          • +5 more
          Mar 1, 2022

          Diamond-Blackfan Anemia, Kostmann's Neutropenia, Shwachman-Diamond Syndrome Trial in Minneapolis (procedure, drug, biological)

          Completed
          • Diamond-Blackfan Anemia
          • +2 more
          • Stem cell transplant
          • +4 more
          • Minneapolis, Minnesota
            University of Minnesota Medical Center
          Dec 3, 2017

          Diamond Blackfan Anemia Trial in Manhasset (Sotatercept, Sotatercept with prednisone boost)

          Terminated
          • Diamond Blackfan Anemia
          • Manhasset, New York
            North Shore- LIJ campus of The Feinstein Institute for Medical R
          Nov 22, 2021

          Diamond Blackfan Anemia, Blackfan Diamond Syndrome, DBA Trial in United States (leucine)

          Unknown status
          • Diamond Blackfan Anemia
          • +4 more
          • Phoenix, Arizona
          • +10 more
          Feb 14, 2020